It is a synthetic version of the naturally occurring coagulation protein that is missing or deficient in people with hemophilia A, an ailment that affects about 13, 000 Americans.
22.
Cohen said protein injections to curb hemophilia A represent a market of $ 1 . 6 billion in the United States, more than four times the market for hemophilia B.
23.
The new drug is a synthetic, genetically engineered version of the naturally occurring coagulation protein that is missing or deficient in people with hemophilia A, a condition affecting about 14, 000 Americans.
24.
Its specialty is providing physicians with DNA tests for people who may be carriers of rare inherited diseases such as cystic fibrosis, Huntington's disease, Tay-Sachs disease, hemophilia A and sickle cell anemia.
25.
Even so, by getting in with Avigen now, Bayer presumably gets a leg up on a future licensing deal, if and when the Alameda firm makes gene therapy possible for hemophilia A.
26.
For 43 years, Miller has been going to the hospital for treatment of hemophilia A, a disease that prevents his blood from clotting and causes severe bleeding in his joints and body cavities.
27.
Nevertheless, Avigen is doing research on delivering the Factor VIII gene with the adeno-associated virus, and expects to seek permission from the FDA to begin a clinical trial in hemophilia A next year.
28.
The company already has an FDA-approved recombinant product on the market for patients with the more common Hemophilia A . Those patients suffer from the absence of a different naturally occurring blood factor.
29.
Avigen is already performing animal tests of a gene therapy for the more common form of hemophilia A . The company hopes to begin testing this new gene therapy on human patients in 2001.
30.
Such X-linked Mendelian diseases include Duchenne muscular dystrophy ( DMD ), and hemophilia A and B, which are rarely seen in females because the offspring is unlikely to inherit two copies of the recessive allele.
How to say hemophilia a in Hindi and what is the meaning of hemophilia a in Hindi? hemophilia a Hindi meaning, translation, pronunciation, synonyms and example sentences are provided by Hindlish.com.
